CRISPR Restores Muscle Function in Mice with Congenital Muscular Dystrophy

Diana Kwon, The Scientist, 17 July 2017,

A new study published in Nature Medicine ( has demonstrated the potential for CRISPR to restore muscle function in congenital muscular dystrophy type 1A.  Researchers used CRISPR gene editing to cut the DNA in two places, allowing the aberrant region to be removed during DNA repair – effectively creating a normal splice.

Author: Advanced Analytical

Advanced Analytical Technologies, Inc. (AATI) simplifies complex genomics workflows to accelerate research and discovery in pharmaceuticals, life science, biofuels, biotechnology and healthcare.

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