CRISPR could provide relief for sickle-cell anemia patients

Heidi Ledford, Nature News, 12 October 2016 http://www.nature.com/news/crispr-deployed-to-combat-sickle-cell-anaemia-1.20782

Sickle cell anemia is the result of a single base change; however, treatments have been limited.  Now researchers out of UC-Berkeley have reported being able to correct the sickle mutation in up to 25% of cells taken from sickle cell patients.   The modified cells were introduced into mice where, despite the initially positive results, only 5% where able to produce normal hemoglobin, demonstrating that a clinical treatment could still be years away.

Author: Advanced Analytical

Advanced Analytical Technologies, Inc. (AATI) simplifies complex genomics workflows to accelerate research and discovery in pharmaceuticals, life science, biofuels, biotechnology and healthcare.

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